Vol 11, N°1
Child and Adolescent Psychiatry
Past issues
Contributors
How to publish
Contributions and comments
Home
Alert
To print this page in good conditions, please select the "Landscape" mode of your printer.
|
Select and print
|
Autism spectrum disorders
utism, also referred to as autistic disorder (des-
ignated as OMIM #209850, by Online Mendelian
Inheritance in Man, an online database of human genes
and genetic phenotypes), is a developmental neuropsy-
chiatric disorder that was first described in 1943 by Dr
Leo Kanner.
1
DSM-IV (
Diagnostic and Statistical
Manual, 4th Edition
,American Psychiatric Association),
or similar criteria are used for diagnosis of autism and
other disorders in this spectrum, referred to as the per-
vasive developmental disorders (PDD). DSM-IV crite-
ria for autism include onset by age 3, impairments in
social interaction and in social communication, as well
as repetitive and stereotypic patterns of behaviors or
restricted interests. Asperger syndrome represents a
higher-functioning form of ASD. Pervasive developmen-
tal disorder-not otherwise specified (PDD-NOS) also
involves deficits in all three domains (social interaction,
social communication, characteristic behaviors/inter-
ests), but the deficits do not reach threshold criteria for
an autism diagnosis. In this review, Asperger syndrome,
T r a n s l a t i o n a l r e s e a r c h
A
Copyright © 2009 LLS SAS. All rights reserved
www.dialogues-cns.org
Multiple rare variants in the etiology of
autism spectrum disorders
Joseph D. Buxbaum, PhD
Keywords:
pervasive developmental disorder; autism spectrum disorder; gene-
tics; association; susceptibility locus
Author affiliations:
Laboratory of Molecular Neuropsychiatry, Seaver
Autism Center for Research and Treatment, Departments of Psychiatry,
Neuroscience, and Genetics and Genomic Sciences, Mount Sinai School of
Medicine, New York, NY, USA
Address for correspondence:
Joseph D. Buxbaum, Department of Psychiatry,
One Gustave L. Levy Place, Box 1668, New York, NY 10029, USA
(e-mail: joseph.buxbaum@mssm.edu)
Recent studies in autism spectrum disorders (ASDs) sup-
port an important role for multiple rare variants in these
conditions. This is a clinically important finding, as, with
the demonstration that a significant proportion of ASDs
are the result of rare, etiological genetic variants, it
becomes possible to make use of genetic testing to sup-
plement behavioral analyses for an earlier diagnosis. As
it appears that earlier interventions in ASDs will produce
better outcomes, the development of genetic testing to
augment behaviorally based evaluations in ASDs holds
promise for improved treatment. Furthermore, these
rare variants involve synaptic and neuronal genes that
implicate specific pathways, cells, and subcellular com-
partments in ASDs, which in turn will suggest novel ther-
apeutic approaches in ASDs. Of particular recent inter-
est are the synaptic cell adhesion and associated
molecules, including neurexin 1, neuroligin 3 and 4, and
SHANK3
, which implicate glutamatergic synapse abnor-
malities in ASDs. In the current review we will overview
the evidence for a genetic etiology for ASDs, and sum-
marize recent genetic findings in these disorders.
© 2009, LLS SAS
Dialogues Clin Neurosci.
2009;11:35-43.